Which would be a better candidate for gene therapy?

a genetic disorder which results from the lack of a blood enzyme that is secreted by bone marrow cells

or

a disease that occurs when nerve cells are unable to produce a particular enzyme

and why?

Related posts:

1. In gene therapy like for that of SCID where do they change the dna?
2. blood cells that have defective genes can be treated with gene therapy, but as they hv limited lifespan (cont)?
3. What complications can arrise when the subjects of gene therapy try to have kids?
4. What are the ethical concerns when dealing with gene therapy?
5. why are bone marrow stem cells ideally suited as targets for gene therapy?

One Response to “Which would be a better candidate for gene therapy?”

1. Matthew says:

   May 18, 2011 at 4:51 pm

   In my personal opinion, it would be better to choose the Nerve Cells option.

   In this situation, a protein in the form of an enzyme is being produced. So, if you applied gene therapy, perhaps this might altar the protein that is being manufactured or perhaps stop it altogether.

   The Bone Marrow experiment would be much more difficult to do and wouldn’t produce better results when compared to the Nerve Cell experiment.

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